Effect of Nusinersen on Adults With Spinal Muscular Atrophy

Study Identifier:
18-0149
ClinicalTrials.gov Identifier:
NCT03878030
EudraCT Identifier:
N/A
EU CT Number:
N/A
Sponsor:
Northwell Health
Study Complete

Study Details

Medical Condition
  • All Spinal Muscular Atrophies
Study Drug
  • Drug: nusinersen
Date
Apr 2019 - Jul 2021
Patient Requirements
Sex: Female & Male
Age: 18 - 60 Years
Requirements Information
Inclusion and Exclusion Criteria
Inclusion Criteria
  • Genetically confirmed 5q SMA
  • ability to access intrathecal space for nusinersen injection
Exclusion Criteria
  • Renal impairment
  • thrombocytopenia
  • inability to access intrathecal space by CT or flouro guided injection

Protocol Summary

Observational study of adult patients with spinal muscular atrophy types 2 and 3 receiving nusinersen

Trial Locations

Location
Status
Location
Northwell Health Neuroscience
Great Neck, New York, United States, 11021
Status
N/A

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